Orchard Therapeutics

Leslie Meltzer, Ph.D., Chief Medical Officer 

Oct. 12 | 4:15pm | UBC Ballroom 

London, UK 


In-person Presentation 

At Orchard Therapeutics, our vision is to end the devastation caused by genetic and other severe diseases. We aim to do this by discovering, developing, and commercializing new treatments that tap into the curative potential of hematopoietic stem cell (HSC) gene therapy. In this approach, a patient’s own blood stem cells are genetically modified outside of the body and then reinserted, with the goal of correcting the underlying cause of disease in a single treatment. In 2018, the company acquired GSK’s rare disease gene therapy portfolio, which originated from a pioneering collaboration between GSK and the San Raffaele Telethon Institute for Gene Therapy in Milan, Italy. Today, Orchard is advancing a pipeline spanning preclinical, clinical, and commercial stage HSC gene therapies designed to address serious diseases where the burden is immense for patients, families, and society and current treatment options are limited or do not exist. 


By using this website you agree to accept our Privacy Policy and Terms & Conditions