22 Jul PTC Therapeutics
Matt Klein, M.D., Chief Development Officer
South Plainfield, NJ
PTC Therapeutics is an industry leader in the discovery, development, and commercialization of medicines for the treatment of rare disorders. For over 20 years, PTC has been pursuing innovative technologies and therapies to develop and provide access to clinically-differentiated medicines for patients living with rare disorders. PTC believes that by using proven scientific technologies, they can find innovative ways to treat rare disorders to create more shared moments and opportunities for patients and their families. Patients are at the center of everything PTC does – they work closely with patient advocacy groups, patients, and caregivers to better understand their specific situation, which helps PTC develop treatments and programs to address the needs of the rare disorder community. Currently, PTC is at the forefront of a new and transformative era of gene therapy, using a targeted gene therapy platform to develop treatments for devastating rare disorders.