19 Jul Center for Gene Therapy at the Abigail Wexner Research Insitute, Nationwide Children’s Hospital
Matthew McFarland, Ph.D., Vice President of Commercialization and Industry Relations
Oct. 11 | 1:15pm | Ecolab Life Sciences Ballroom
The Center for Gene Therapy is focused on the translational development of gene therapies for inherited disorders. The Institute has a long history of engagement with biotech partners, and research at the center has led to approved therapies for spinal muscular atrophy and Duchenne muscular dystrophy. A significant number of projects are underway at various stages of preclinical development, including ones directed towards new or improved approaches to DMD, limb-girdle muscular dystrophies, inherited neuropathies, and degenerative and developmental disease of the central nervous system.