22 Jul GENETHON
Imen Mestiri, Ph.D., Business Development Manager
Oct. 8 | 9:15am | FLW Ballroom G
Évry, France
(Private)
A pioneer in the discovery and development of gene therapies for rare diseases, Genethon is a unique non-profit organization created by a patient association, the AFM- Telethon. A first gene therapy drug, to which Genethon contributed, has obtained marketing for spinal muscular atrophy. With 200+ scientists and professionals, Genethon is pursuing its mission to bring life-changing therapies to patients suffering from rare genetic diseases. Thirteen products resulting from Genethon’s research are in clinical trials for liver, blood, immune system, muscle and eye, diseases. A further seven products are in the preparation phase for clinical trials over the next five year.